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Rare Disease

Rare Disease

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In general, the main challenges in creating and implementing orphan drugs result from the rarity, heterogeneity and the complex patient management inherently in rare conditions. CD BioSciences' clinical trial development service is your preferred rare disease CRO to eliminate the biggest obstacles in medicine. With our practical experience and understanding of rigorous methodology, we can come up with one-stop clinical research designs and data analysis strategies that are suitable for the challenges of rare diseases.

Rare Disease Clinical Study Experience

Clinical trials of rare diseases require innovative thinking and wise adjustments in the process. For the success of rare disease research, there is usually no standard trial design or formula. Therefore, working with a CRO with extensive experience and understanding of rare disease drug and device development can effectively remove many of the obstacles that may exist. CD BioSciences is committed to bringing years of therapeutic experience, strategic regulatory guidance and innovative execution to drive your program from preclinical concept to clinc.

CD BioSciences focuses on the following rare disease areas, but not limited to:

Rare Disease Clinical Study Experience
  • Acute Myeloid Leukemia (AML)
  • ADA-Deficient SCID
  • Biliary Tract Cancer
  • Crigler-Najjar Syndrome
  • Cutaneous T-Cell Lymphoma
  • Lamellar Ichthyosis
  • Leber Hereditary Optic Neuropathy
  • Leukemia/Myelodysplastic Syndrome (MDS)
  • Liver/Biliary/Pancreas Cancer
  • Lymphoma, Non Hodgkin Lymphoma (NHL)
  • Mesothelioma
  • Midgut Carcinoid Tumors
  • Niemann Pick Type C Disease
  • Positive Chronic Myelogenous Leukemia
  • Prev. of Acute Graft Vs Host Disease (aGvHD)
  • Retinitis Pigmentosa (RP)
  • Scleroderma
  • Spinal Muscular Atrophy
  • Urea Cycle Disorders
  • Wilson's Disease
  • Wiskott-Aldrich Syndrome
  • Acute Lymphoblastic Leukemia (ALL)
  • Angelman Syndrome
  • Arginase Deficiency
  • Mucopolysaccharidosis VI (Maroteaux-Lamy Syndrome)
  • Sickle Cell Disease
  • Soft Tissue Sarcoma
  • Thrombotic Microangiopathy
  • Vasculitis
  • Von Willebrand Disease
  • Velocardiofacial Syndrome, Psychosis
  • Duchenne Muscular Dystrophy
  • Fabry Disease
  • Farber's Disease
  • Focal Segmental Glomerulosclerosis (FSGS)
  • Gaucher Type 1
  • Hereditary Angioedema (HAE)
  • Hunter Syndrome (Mucopolysaccharidosis II, MPS II)
  • Huntington's Disease
  • Mucopolysaccharidosis I (MPS I)
  • Niemann-Pick Disease
  • Neuroblastoma
  • Neuromyelitis Optica Spectrum Disorder (NMO)
  • Pheochromocytoma and Paraganglioma
  • Pompe Disease
  • Sanfilippo Syndrome (Mucopolysaccharidosis III, MPS-III)
  • Sarcoma
  • Acromegaly
  • Active Systemic Onset Juvenile Idiopathic Arthritis
  • Amyotrophic Lateral Sclerosis
  • Cystic Fibrosis
  • Duchenne Muscular Dystrophy
  • Gaucher's Disease
  • Growth Hormone Insensitivity Syndrome
  • Hemophagocytic Lymphohistiocytosis
  • Idiopathic Pulmonary Fibrosis
  • Idiopathic Thrombocytopenic Purpura
  • Kawasaki Disease
  • Lambert-Eaton Myasthenic Syndrome
  • Lymphoma
  • Mad Cow Disease
  • Mucopolysaccharidosis I (Hurler Syndrome)
  • Mucopolysaccharidosis II (Hunter Syndrome)

Experience in Recruiting Patient Populations

We also work with a variety of companies who provide global medical resources in recruiting professional patient populations to meet complex clinical challenges along the path to a successful clinical transformation. It is worth noting that our expertise is not only in recruiting professional patient populations, but also in retaining them for long-term research, which is critical for advancing a seamless and integrated clinical research.

Schema of ARG1 and NOS2 metabolic pathways

Explore Our Clinical Services for a Complete Picture by Stage:

CD BioSciences' scientists are dedicated to bringing together years of valuable experience to help our clients shorten the clinical trial journey. For further details, please don't hesitate to contact us.

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